Becker's Hospital Review: The future GLP-1 might be a gene therapy: Report
In common speech, "gene" is often used to refer to the hereditary cause of a trait, disease, or condition—as in "the gene for obesity." Speaking more precisely, a biologist might refer to an allele or a mutation that "has been implicated in" or "is associated with" obesity.
NPR: Gene therapy for a rare type of deafness shows lasting results
Researchers say a gene therapy allowed deaf children and adults as old as 32 to hear for the first time. The benefits have persisted for more than two years for some patients.
Fierce Biotech: Eying 3 approvals in 2 years, Ocugen’s CEO wants to bring gene therapy to the masses
To Ocugen CEO Shankar Musunuri, Ph.D., most gene therapy biotechs today lack vision. | Many gene therapy outfits focus on technical advances, Ocugen CEO Shankar Musunuri, Ph.D., said, meaning they ...
Eying 3 approvals in 2 years, Ocugen’s CEO wants to bring gene therapy to the masses
Labiotech.eu: The future of cell & gene therapy: Key trends to watch
Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.
Managed Healthcare Executive: Gene therapy may be a once-in-lifetime treatment. That gives some patients and providers pause and a willingness to ‘wait it out’ until a better therapy comes along | AMCP ...
Pfizer announced in February 2025 that it was taking Beqvez (fidanacogene elaparvovec), its gene therapy for hemophilia B, off the market, and BioMarin is pulling Roctavian (valoctocogene roxaparvovec ...
Gene therapy may be a once-in-lifetime treatment. That gives some patients and providers pause and a willingness to ‘wait it out’ until a better therapy comes along | AMCP ...
FierceBiotech: Regenxbio posts clean safety profile for DMD gene therapy as pivotal data loom
Regenxbio has guided its Duchenne muscular dystrophy (DMD) gene therapy candidate through another test, reporting a clean safety profile and functional improvements as it heads toward pivotal data.
Regenxbio posts clean safety profile for DMD gene therapy as pivotal data loom
As GLP-1 pills for weight loss enter the U.S. market, some pharmaceutical companies are testing the possibility of a gene therapy to stimulate GLP-1 production, The Washington Post reported Jan. 24.
Managed Healthcare Executive: Gene therapy brims with promise. The reality has been less rosy for some therapies | AMCP Annual 2026
Gene therapy brims with promise. The reality has been less rosy for some therapies | AMCP Annual 2026
Yahoo: Doctors awarded science ‘Oscar’ for curing inherited blindness with gene therapy
Three scientists have won the 2026 Breakthrough Prize for developing Luxturna — the world's first FDA-approved gene therapy for inherited blindness.
The Philadelphia Inquirer on MSN: Philly scientists win 2026 Breakthrough Prize for developing gene therapy for blindness
Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a ...
Philly scientists win 2026 Breakthrough Prize for developing gene therapy for blindness
MSN: First-ever experimental gene therapy seeks to restore vision by rejuvenating eye neurons
Life Biosciences is pushing cellular rejuvenation into the clinic with ER-100, an experimental gene therapy designed to restore vision by reviving damaged neurons in the eye. Rather than slowing ...
First-ever experimental gene therapy seeks to restore vision by rejuvenating eye neurons
Key takeawaysResults from a UCLA-led clinical trial for sickle cell disease reveal the unique challenges of treating blood disorders with gene therapy ...
The Print on MSN: Cancer therapy may soon skip the lab step — and cut costs
Cancer therapy may soon skip the lab step — and cut costs
Seeking Alpha: Neurogene: Stock Soars On FDA Designation For Rett Gene Therapy - I'd Remain Cautious
Neurogene: Stock Soars On FDA Designation For Rett Gene Therapy - I'd Remain Cautious
GeneCards®: The Human Gene Database GeneCards is a searchable, integrative database that provides comprehensive, user-friendly information on all annotated and predicted human genes. The knowledgebase automatically integrates gene-centric data from ~200 web sources, including genomic, transcriptomic, proteomic, genetic, clinical and functional information.
Search GeneCards Free for academic non-profit institutions. Other users need a Commercial license
CIViC Summary for MDM2 Gene GeneCards Summary for MDM2 Gene MDM2 (MDM2 Proto-Oncogene) is a Protein Coding gene. Diseases associated with MDM2 include Lessel-Kubisch Syndrome and Accelerated Tumor Formation. Among its related pathways are Cell-cell junction organization and Regulation of activated PAK-2p34 by proteasome mediated degradation.
Complete information for YBX1 gene (Protein Coding), Y-Box Binding Protein 1, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Complete information for HK2 gene (Protein Coding), Hexokinase 2, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Complete information for ACSL4 gene (Protein Coding), Acyl-CoA Synthetase Long Chain Family Member 4, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Complete information for SQSTM1 gene (Protein Coding), Sequestosome 1, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Complete information for CYP1A2 gene (Protein Coding), Cytochrome P450 Family 1 Subfamily A Member 2, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Summaries for HIF1A Gene NCBI Gene Summary for HIF1A Gene This gene encodes the alpha subunit of transcription factor hypoxia-inducible factor-1 (HIF-1), which is a heterodimer composed of an alpha and a beta subunit.
Complete information for LPCAT1 gene (Protein Coding), Lysophosphatidylcholine Acyltransferase 1, including: function, proteins, disorders, pathways, orthologs, and expression. GeneCards - The Human Gene Compendium
Genes NCBI's Gene resources include collections of curated nucleotide sequences used as references, sequence clusters to predict and study homologs, and various databases and tools for the study of gene expression. How to Find the function of a gene or gene product Find published information about a gene Find a homolog for a gene in another ...
In biology, the word gene has two meanings. The Mendelian gene is a basic unit of heredity. The molecular gene is a sequence of nucleotides in DNA that is transcribed to produce RNA.